Health on MSN1mon
What To Know About Duchenne Muscular Dystrophy (DMD)
DMD is an inherited (passed down ... a sign of muscle cell damage. A muscle biopsy (tissue sample) is usually taken from the ...
The American Journal of Managed Care3d
EMBARK Data Show Continued Improvements With DMD Gene Therapy
Data from the EMBARK trial of delandistrogene moxeparvovec in patients with Duchenne muscular dystrophy (DMD) show that ...
Yahoo Finance1mon
Solid Biosciences’ stock soars on early success in DMD gene therapy trial
The company announced 90-day biopsy data from the Phase I/II ... in all evaluated clinical biomarkers of muscle damage associated with DMD provide preliminary evidence of a beneficial effect ...
Medscape19d
Association of Duchenne Muscular Dystrophy With Autism Spectrum Disorder
The diagnosis of Duchenne muscular dystrophy was made in all patients on the basis of the clinical history and the absence or near-absence of the dystrophin protein on muscle biopsy. In addition ...
Benzinga.com1mon
Solid Biosciences Stock Surges On Upbeat Duchenne Muscular Dystrophy Gene Therapy Data
Duchenne muscular dystrophy (DMD ... which helps keep muscle cells intact. Interim 90-day biopsy data reported in the first three participants showed an average microdystrophin expression of ...
Business Wire16d
Italfarmaco Provides Overview on Givinostat as Treatment for Duchenne Muscular Dystrophy: Progress in Global Access, Regulatory Milestones and Clinical Trials
3 Dystrophin is a critical component of the dystrophin-associated protein complex (DAPC) which supports the strength, stability, function and repair of muscle cells. In DMD, muscle fibres are ...