Speakers from the Muscular Dystrophy Association (MDA) highlighted 75 years of progress in understanding and treating ...

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

The mother of a teenage boy, with muscular dystrophy, said her son hasn’t been able to leave their Oakland home for almost a ...

NEW YORK, NY / ACCESS Newswire / March 24, 2025 / Bronstein, Gewirtz & Grossman, LLC is investigating potential claims on ...

Sarepta Therapeutics announced that a patient with Duchenne muscular dystrophy who received Elevidys (delandistrogene moxeparvovec-rokl) died following treatment.

Korean researchers have proposed a new treatment strategy that can increase the effectiveness of the genetic rare disease ...

Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...

A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...

One of the major highlights of the Muscular Dystrophy Association (MDA) Clinical & Scientific Conference is that invaluable networking opportunities can help clinicians elevate their own best ...

Kyle Albertson, an FFA alumnus and Purdue graduate, shares how FFA prepared him for a career in business despite his ...

Researchers focused on Myotonic Dystrophy 1 heart problems are testing a novel approach to restore normal function.

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...