Scary diagnosis: Young patients in Maine helped to brave their worst medical fears
PORTLAND, Maine (WGME) -- MaineHealth Barbara Bush Children's Hospital is crucial to so many families, some of which are ...
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First patient dosed in Phase Ib Pompe disease trial
Aro Biotherapeutics has dosed the first patient in a Phase Ib trial of ABX1100, a novel treatment for late-onset Pompe disease (LOPD), a rare inherited disorder that causes progressive muscle ...
The Sheridan Press9d
Nonprofit organizes show to support child with Pompe disease
Compete for a Cause will host a 16-act talent competition at 6 p.m. on April 5 at Sheridan College for Pompe Disease patient ...
AI tool creates detailed 3D map of mouse brain metabolism, portending advances in Alzheimer's research
It is a detailed view of the brain like never seen before. In a significant technological leap, University of Florida ...
The American Journal of Managed Care13d
For Neuromuscular Disease Community, an Era of Opportunities and Threats
Robert Califf, MD, former commissioner of the FDA, delivered a keynote address at the 2025 Muscular Dystrophy Association ...