The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...

Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the ...

FDA aligned on single-arm Phase 3 study to support potential accelerated and full approval On track to dose first patient in Phase 3 trial in second half of 2025 LONDON, Feb. 03, 2025 (GLOBE NEWSWIRE) ...

The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

LEXINGTON, Mass. - uniQure N.V. (NASDAQ: NASDAQ:QURE), a gene therapy company with a market capitalization of $767 million, ...

AI could deliver substantially greater efficiencies in cell and gene therapy manufacturing and enable more patients to ...

Previous research has shown that voretigene neparvovec administered subretinally early in childhood for RPE65-mediated ...

President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program to ...

BENGALURU: Bengaluru-based Narayana Nethralaya is developing gene therapy solutions that could drastically reduce the cost of ...

NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...

The bill would implement a moratorium for a decade. “I am not against vaccination in any way,” the freshman lawmaker said.

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...