A 12-year-old Newry boy living with Duchenne Muscular Dystrophy (DMD) has had the opportunity to meet with Northern Ireland’s ...

Capricor Therapeutics (CAPR) announced on Monday that it has completed a mid-cycle review meeting with the U.S. Food and Drug ...

Capricor Therapeutics said on Monday the U.S. Food and Drug Administration (FDA) plans to convene a panel of outside experts ...

Practical pain relief strategies for people with DMD and their caregivers, covering daily care, medications, and emotional ...

From STAT’s Adam Feuerstein: The FDA informed Capricor Therapeutics that a meeting of outside experts will be convened to ...

It’s a devastating diagnosis that changes a child’s life — and their family’s — forever. Duchenne Muscular Dystrophy, or DMD, is a rare and fatal genetic disease that primarily affects boys, slowly ...

A Tucson preschool teacher spotted a developmental quirk in a little boy who was then able to get early treatment for ...

One Western New Yorker had a life-changing moment when he got the chance to take the national stage at the NFL draft on April ...

While right-wing populism surges in some of the world’s leading democracies, Chile’s leftist government is rushing in the ...

At age 2, Cal Carr was already reaching developmental milestones later than expected — and then she started regressing.

Gene therapy has emerged as a promising approach to previously untreatable conditions, including Duchenne muscular dystrophy (DMD), a progressive disorder caused by DMD mutations that leads to early ...

The symposium took place on 18 th March 2025, as part of the Muscular Dystrophy Association (MDA) Clinical & Scientific ...