In December 2023, through the development efforts of CRISPR Therapeutics and Vertex Pharmaceuticals, their decades-long ...

Accumulation of clots causes some of the most severe symptoms of sickle cell disease, including strokes, kidney failure, ...

A cutting-edge gene therapy has been approved for NHS use for some patients with severe sickle ... for chemistry in 2020. It works by editing the faulty gene in a patient’s own stem cells.

Sickle cell disease is a group of inherited blood disorders that ... Emmanuelle Charpentier and Jennifer A. Doudna, the Nobel Prize in Chemistry in 2020. Exa-cel, also called Casgevy, involves taking ...

It is believed around 1,700 people could be eligible for the treatment, while the NHS estimates around 50 people a year will ...

This achievement follows Bahrain’s landmark decision on 2 December 2023 to become the second country globally and the first ...

describes studies in which humanized sickle cell mice topically treated with Vascarta's transdermal curcumin gel formulation ("VAS-101") experienced reduced pain and inflammation along with ...

But not if you suffer from sickle cell disease, which affects nearly 8 million people worldwide, most in sub-Saharan Africa. In the UK, approximately 17,500 people have sickle cell disease and 300 ...

But not if you suffer from sickle cell disease, which affects nearly eight million people worldwide, most in sub-Saharan Africa. In the UK, approximately 17,500 people have sickle cell disease and 300 ...