Medically reviewed by Smita Patel, DO Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed ...

Solid Biosciences’ gene therapy uses a shortened version of the dystrophin protein, which is engineered to mimic the key functions of full-length dystrophin and allows it be delivered more effectively ...

Health Minister Mike Nesbitt is to push the Belfast Trust on why it won’t make a new drug to treat muscular dystrophy ...

Leah Messer is opening up about navigating her daughter Ali's muscular dystrophy as the 15-year-old takes a big step in her life: high school. In an interview with TooFab ahead of the new season ...

2025 could be a breakout year for the Duchenne muscular dystrophy space. Although several therapies have entered the market in recent years, there is still considerable unmet need for the 15,000 ...

According to NBA insider Marc Stein, there is "optimism" that Dallas Mavericks star Luka Dončić will return to the team from his calf injury before the NBA All-Star break. Dallas' final game ...

NEW YORK – Belief BioMed announced Wednesday that the US Food and Drug Administration has cleared its investigational new drug application enabling it to begin testing its gene therapy candidate for ...