Avidity Biosciences, Inc. , a biopharmaceutical company committed to delivering a new class of RNA therapeutics called Antibody Oligonucleotide Conjugates (AOCstm), today announced that the Japan ...

Mexiletine appears to be safe and is likely an effective treatment for managing symptoms of myotonia (delayed muscle relaxation after a contraction) in people wit ...

Trine Lise Frost is a veterinary nurse at a shelter in Australia who shares some of the stories of the animals she treats on ...

Fainting goats aren’t just clumsy they’re born with a rare condition called myotonia congenita. When startled, their muscles temporarily stiffen, causing them to fall over in dramatic fashion.

Use of DYNE-101 is leading to improvements in muscle, and specifically finger, function in myotonic dystrophy type 1 patients, new data show.

Arrakis’s DM1 drug program represents a rationally designed small molecule genetic medicine directed at a pathogenic RNA to achieve reversal of myotonia in an animal model of DM1. Utilizing the ...