News

rarediseaseadvisor18d
I Am Going to WODC to Advocate on Behalf of Rare Disease Patients
I live with indolent systemic mastocytosis (SM) and it’s my goal to provide hope to anyone living with a rare disease. I use my own stories to do this, but I feel I can do more. I want to advocate for ...
Business Insider19d
Leqembi®∇ (lecanemab) is the First Medicine that Slows Progression of Early Alzheimer’s Disease to be Authorized in the European Union
In the European Union (EU), lecanemab is indicated for the treatment of adult patients with a clinical diagnosis of mild cognitive impairment and mild dementia due to Alzheimer’s disease (early ...
BioPharma Dive19d
Startup Glycomine raises $115M to push rare disease drug deeper into testing
The company’s approach is somewhat akin to the enzyme replacement therapies used to treat lysosomal storage disorders like Fabry or Pompe disease. Glycomine’s therapy is replacing a missing sugar ...
Business Insider24d
Odylia Therapeutics drives commitment to rare disease drug development through Rare Disease Day event
BOSTON, MA, April 10, 2025 (GLOBE NEWSWIRE) -- Odylia Therapeutics (Odylia) a nonprofit biotechnology company dedicated to expediting drug development for rare diseases, hosted a Rare Disease Day ...
9to5google25d
Chrome 135 rolling out edge-to-edge design on Android
As previewed last month, Chrome 135 for Android is rolling out an edge-to-edge design for the bottom of your screen. As you scroll down a webpage, Android’s gesture navigation bar is no longer ...
inkbotdesign.com25d
Top 10 Iconic Band & Music Logos for Design Inspiration
The top 10 iconic band and music logos that can inspire your own design. Perfect for business owners seeking creative inspiration. Get inspired! In our visually-driven world, a killer logo is ...
rarediseaseadvisor26d
FDA Approves First Ever Treatment for IgG4-RD
Although the exact mechanism of action of inebilizumab-cdon remains unknown, clinical data have shown significant benefits in reducing disease activity. The US Food and Drug Administration (FDA) has ...
BGR26d
This iPhone 17 Air dummy shows off Apple’s impossibly thin new design
Following Bloomberg‘s Mark Gurman’s report that the two-toned back color leaks for the iPhone 17 Pro were wrong, new iPhone 17 Air dummies show off the mono-color design we’re now expecting.
Mena FN26d
Geneventiv Announces Global Licensing Agreement For Universal Gene Editing Therapy For Infantile Onset And Late Onset Pompe Disease
(MENAFN- PR Newswire) Pompe disease results from a deficiency of an enzyme called acid-alpha-glucosidase (GAA), leading to massive lysosomal glycogen buildup in striated muscle, resulting in ...
Yahoo Finance26d
GeneVentiv Announces Global Licensing Agreement for Universal Gene Editing Therapy for Infantile Onset and Late Onset Pompe Disease
Pompe disease results from a deficiency of an enzyme called acid-alpha-glucosidase (GAA), leading to massive lysosomal glycogen buildup in striated muscle, resulting in respiratory failure ...
Metro26d
Robbie Williams reveals he contracted ‘a 17th-century pirate disease’ and details health struggles
‘A 17th-century pirate disease,’ Robbie told The Mirror. He added that he was getting incredibly thin, but his body dysmorphia made concerned comments from friends and family sound like ...
Morningstar27d
GeneVentiv Announces Global Licensing Agreement for Universal Gene Editing Therapy for Infantile Onset and Late Onset Pompe Disease
The therapy has been designated GENV-002. Pompe disease results from a deficiency of an enzyme called acid-alpha-glucosidase (GAA), leading to massive lysosomal glycogen buildup in striated ...